Neurotherapeutics Course
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Course Lecture Videos
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2021 Course Offering of Training in Neurotherapeutics Discovery and Development for Academic Scientists



Session 1: Target and Pathway Interrogation
James Inglese, PhD, National Center for Advancing Translational Sciences, NIH

Session 2: Biology Basics for Identifying Hits
William Janzen, BS, Epizyme, Inc.

Session 3: Moving from Hit to Lead to Clinical Candidate
James Barrow, PhD, Johns Hopkins School of Medicine

Session 4: Antibody-Based Therapies
Gai Ayalon, PhD

Session 6: Intellectual Property
Jeffrey W. Childers, PhD

​Session 7: Alternative Approaches to Lead Generation
Sam J. Enna, PhD, The University of Kansas

Session 8: ADME
Kennan Marsh, PhD, AbbVie

Invited Guest Speaker: The Story of Risdiplam/Everysdi 
Alexander Stephan, PhD, Roche Pharma Research

Session 10: Rigor in Translational Drug Discovery and Development
Shai Silberberg, PhD, NIH/NINDS

Session 11: Toxicology
Adaline Smith, PhD, DABT, Ironwood Pharmaceuticals

Session 12: IND Enabling Studies and Preparation of the IND
Edward Spack, PhD, Medared

Session 13: Formulation and Route of Administration
James Cloyd III, PharmD, University of Minnesota

​Session 13: Formulation and Route of Administration
Maureen Donovan, PhD, University of Iowa

Session 13: Antisense Oglionucleotides
Gene Liau, PhD, Stoke Therapeutics

​Session 14: Clinical Considerations in the Non-Clinical Phase of Drug Discovery and Development
James Vornov, MD, PhD, Johns Hopkins School of Medicine and Medpace

​Session 15: Funding Academic Drug Discovery Research
Charles L. Cywin, PhD, NIH/NINDS

Lecture Videos from 2018 Course Offering
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